Appointment in February

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Offline Sharmin

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Appointment in February
« on: January 07, 2009, 10:19:14 PM »
Little A has an appointment in Oakland mid February.  Once again I am making a list of questions and concerns.  If any of you have questions I will do my best to get answers for you. 

Manal, you had a question last time which I didn't get until I got back - was it about pulmonary hypertension?

Sharmin
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Offline nice friend

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Re: Appointment in February
« Reply #1 on: January 11, 2009, 09:18:56 AM »
Sharmin,
i have a question that is abt combination therapy of Exjade + desferal ,
when the combination therapy of exjade+desferal will be proved to secure ??..
when trials report will be available of exjade+desferal combination therapy ??..
wat is his opinion abt gene therapy ??

take care
Best regards
umair
Sometimes , God breaks our spirit to save our soul.
Sometimes , He breaks our heart to make us whole.
Sometimes , He sends us pain so we can be stronger.
Sometimes , He sends us failure so we can be humble.
Sometimes , He sends us illness so we can take better care of our selves.
Sometimes , He takes everything away from us so we can learn the value of everything we have.

===========
Umair

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Offline Zaini

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Re: Appointment in February
« Reply #2 on: January 11, 2009, 09:56:31 AM »
Is there any possibility or any trial (even individual),for ferriprox and exjade going on?

Zaini.
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Offline Lena

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Re: Appointment in February
« Reply #3 on: January 11, 2009, 10:07:39 AM »
Yes Zaini,

in my Blood Transfusion Unit, there is a  little girl of about 8 years old who  is on a trial of combination ferriprox and exjade but it is too recent to publish any results.
If I learn something I ll let you know.

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Offline Manal

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Re: Appointment in February
« Reply #4 on: January 11, 2009, 11:17:08 AM »
Sharmin

Thanks a lot dear, yes it was about PHT but i can not recall the nature of the question, i will search for the old post and let you know, thanks my friend :hugfriend


Zaini
I remember that Dr. Piga in Singapore didn't recommend at all combining ferriprox and exjade togather since they both have their side effects in the same area and this put a big negative load on the body

manal

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Offline Zaini

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Re: Appointment in February
« Reply #5 on: January 11, 2009, 11:49:02 AM »
Lena,

Please post any details you find,how long has she been taking them both?

Manal,

Yes that's what we have heard till now,but like we have seen people doing desferal and exjae together,may be ferriprox and exjade will become a possibility too,and it will be very helpful for people with very high iron overload.

Zaini.
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Offline Sharmin

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Re: Appointment in February
« Reply #6 on: January 11, 2009, 05:28:27 PM »
Hi Zaini,

I will definitely ask the question.  My personal opinion is that since both L1 and exjade remove iron at the tissue and organ level - using desferal in combination can chelate the iron removed from the tissue by either L1 or exjade.  (Desferal does not have the ability to easily get inside tissue to bind an remove iron - but it is very effective at binding iron in the plasma for its removal).   In this way the effect of desferal with either exjade or L1 is synergestic.  L1 or exjade remove iron from tissue - making it available for desferal to remove.  Desferal makes L1 or exjade therapy more effective by quickly removing iron that they have removed from tissue. 

On the surface, it does not appear to me that L1/exjade combination therapy would have synergestic effects since they both remove iron from tissue - and not is as effective as desferal at removing it from the plasma.  The possible benefits that I see are 1) They are both oral - meaning no needles!!  2) L1 removes iron very effectively from the heart, exjade is believed to remove iron from the liver and other organs and together they could possibly remove a lot more iron. 3) L1 does not cause the same spike in SF when one first starts to use it therefore I am assuming that either it removes iron less quickly than exjade or L1 is more capable of excreting iron from the plasma then exjade and in this case it would work well together with exjade.   For these reasons the two may work well in combination.       

My reasons for not thinking that they should be used in combination are: 1) desferal is known to have very few side effects while exjade and L1 are both considered to pose more threat - therefore using them in combination with each other (as compared to using either in combination with desferal) may pose of a risk  2)  exjade may in fact be good at removing iron from the heart as well as other organs - in this case L1 may not be necessary while using exjade to remove cardiac iron overload  3) Desferal requires very few tests to ensure that it is not causing side effects - exjade requires testing every 3 weeks - and L1 requires many tests as well (because of its effect on immune system, joints etc) - therefore if you were using both imagine the number of tests that one would have to have done   (which also shows you how many side effects one is risking). 

These are my thoughts for why one may or may not consider the drugs in combination - it is a great idea - why not use to effective oral drugs together - remove iron and avoid needles!  However the synergestic effects may not be high enough to risk the numerous side effects.  I would like to hear what the experience is for the one patient taking the two drugs in combination - because who knows maybe the two would great together.   I am excited about the possibility of someday using starched desferal with exjade. 

Oakland is not keen on giving L1 to children - because when I asked them about it they had said that they were concerned about its effects on children.  By the way Zaini - this is a great question and provokes a lot of thought - I will be honored to ask it  :hugfriend

Andy, what do you think?

Thank you everyone for your questions - I will take note and please keep asking and praying that little A's tests go well.  We will be repeating the SQUID, T2* and we will be doing a dexa scan for the first time.  I am quite nervous but hopeful that the results will be favorable for my son and show that exjade/desferal combination is safe and effective so that it can benefit everyone else. 

Thanks guys,
Sharmin

Sharmin

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Offline Sharmin

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Re: Appointment in February
« Reply #7 on: January 13, 2009, 05:39:26 AM »
I hope that the tests in Oakland reveal that little A's iron levels are low enough such that he can also stop using desferal - or at the very least such that his desferal dose can be decreased to 2 or 3 times a week.  He only lets us put it on his stomach - and his stomach is quite bruised now.  Because he plays ice hockey (he is skating all of the time) and soccer - his thighs have only muscle and no fat therefore we can't put it on his legs.  His arms are too skinny, and he won't let us put it on his hips.  I am praying that he will get a break from the needles too.   
Sharmin

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Offline Zaini

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Re: Appointment in February
« Reply #8 on: January 13, 2009, 07:36:25 AM »
My all prayers are with Little A  :hugfriend With the strict regimen you have followed i am sure his iron levels must be down. :pray

Little A,

Lets find out your results and then we'll celebrate together  :wink

Zaini.
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Offline nice friend

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Re: Appointment in February
« Reply #9 on: January 13, 2009, 09:06:03 AM »
hey Lil A ,
when ever i start writing a post to you , a thought blink's in my mind and remind me the movie in whic young blood team rule over the game ( ice hockey ) against the cheater ones ( cheater  use's all that they have to hit the not the strike but the opponent )  thats wh i remember them as cheaters ..... wish you all the best for your Tests especialy SF ..  you are such a brave boy buddy ... and brave boy never fails ... take care of your self and keep playing ice hockey ...

Best Regards
Take Care
Umair
Sometimes , God breaks our spirit to save our soul.
Sometimes , He breaks our heart to make us whole.
Sometimes , He sends us pain so we can be stronger.
Sometimes , He sends us failure so we can be humble.
Sometimes , He sends us illness so we can take better care of our selves.
Sometimes , He takes everything away from us so we can learn the value of everything we have.

===========
Umair

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Offline Manal

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Re: Appointment in February
« Reply #10 on: January 13, 2009, 11:39:21 AM »
Quote
his thighs have only muscle and no fat therefore we can't put it on his legs.  His arms are too skinny, and he won't let us put it on his hips.  I am praying that he will get a break from the needles too.
   

I just pray that all the children of the world and especially children will have an alternative for desferal and have a break from the needles, Ameen :pray :pray :pray :pray :pray :pray

manal

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Offline nice friend

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Re: Appointment in February
« Reply #11 on: January 13, 2009, 12:31:50 PM »
 :pray AMEEN :pray
Sometimes , God breaks our spirit to save our soul.
Sometimes , He breaks our heart to make us whole.
Sometimes , He sends us pain so we can be stronger.
Sometimes , He sends us failure so we can be humble.
Sometimes , He sends us illness so we can take better care of our selves.
Sometimes , He takes everything away from us so we can learn the value of everything we have.

===========
Umair

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Offline Sharmin

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Re: Appointment in February
« Reply #12 on: January 13, 2009, 01:58:38 PM »
Thank you very much my friends - I love you all   :grouphug


My prayers are the same - for all thals to be well without needles.

Sharmin
Sharmin

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Offline Sharmin

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Re: Appointment in February
« Reply #13 on: January 22, 2009, 04:05:24 AM »
I have been hearing that the other patients in the trial are continuing to do well and are being allowed to get off of the desferal - how wonderful it would be to not have to put desferal on anymore!  Dr. Vichinsky told us that the ultimate goal is to get rid of desferal - but another doctor said that eventually we will use mostly exjade but desferal 2 or 3 times a week....I wonder what they will decide when we get there.  I think that if his iron levels are below 600 we can get off of desferal, however I have also heard that one whose iron levels are below 1000 should not be using desferal....  ??? ??? ???

Sharmin
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Offline Zaini

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Re: Appointment in February
« Reply #14 on: January 22, 2009, 06:55:27 AM »
Isn't level of 1000 enough to get rid of desferal?  :-\  Exjade will remove the rest?

Zaini.
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